Tag

Gene therapy

Ultragenyx says EMA validates Sanfilippo gene therapy application
Adrian Kessler · Oct 3, 2026
REGENXBIO reports three-year retinopathy improvement in 6 of 10
Adrian Kessler · Sep 25, 2026
Poseida Therapeutics shares skyrocket on acquisition from pharma-giant Roche
Joseph Morton · Nov 26, 2024